Myotonic dystrophy
Not recruitingStudy on AOC 1001 for Treating Myotonic Dystrophy Type 1 in Patients
Study on AOC 1001 for Treating Myotonic Dystrophy Type 1 in Patients
- Disease:Myotonic dystrophy
- Substances:Humanised Igg1 Monoclonal Antibody Against Tfr1 Conjugated To Double Stranded Sirna Oligonucleotide Against Dmpk Via A Non-Cleavable Linker
Denmark- Participants:0–17 years · 18–64 years
- Substances:Humanised Igg1 Monoclonal Antibody Against Tfr1 Conjugated To Double Stranded Sirna Oligonucleotide Against Dmpk Via A Non-Cleavable Linker
- Sponsor:Avidity Biosciences Inc.












