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uniQure biopharma B.V.
Sponsor

uniQure biopharma B.V.

The Netherlands Paasheuvelweg 25, 1105 BP Amsterdam, The Netherlands

About the sponsor

Research activity in Huntington’s disease focuses on gene therapy and HTT gene lowering strategies for adults with early manifest disease, with attention to striatal delivery and neurological degeneration.

  • HTT gene lowering
  • Striatal delivery
  • Neurodegenerative disease

The clinical work in this area is centered on central nervous system targeting for movement disorder pathology associated with Huntington’s disease.

About Specializations

uniQure biopharma B.V. runs clinical trials in conditions such as Amyotrophic lateral sclerosis, Huntington's disease, among others.

All trials

Ongoing trials

Clinical trials registered by this sponsor – none is enrolling right now.

Condition
Country
City
Type of trial
Recruitment status
Quick filters

2 clinical trials

Amyotrophic lateral sclerosis

Not recruiting
InvestigationalNo placebo
Countries:SwedenSweden
  • Participants:18–64 years · 65+ years
  • Substances:ADENO-ASSOCIATED VIRAL VECTOR SEROTYPE RH10 ENCODING MIRNA AGAINST SOD1 MRNA
  • Sponsor:uniQure biopharma B.V.

Huntington's disease

Not recruiting
InvestigationalNo placebo
Countries:PolandPoland
  • Participants:18–64 years
  • Substances:Ifezuntirgene Inilparvovec
  • Sponsor:uniQure biopharma B.V.

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