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Rare disease

Activated PI3 kinase delta syndrome

  • 4 clinical trials
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4 Clinical trials

Countries:GermanyGermany
  • Participants:18–64 years · Healthy volunteers
  • Substances:Leniolisib Phosphate
  • Sponsor:Pharming Technologies B.V.
Countries:PortugalPortugal
  • Participants:0–17 years
  • Substances:Leniolisib Phosphate
  • Sponsor:Pharming Technologies B.V.
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Leniolisib Phosphate
  • Sponsor:Pharming Technologies B.V.
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years
  • Sponsor:Pharming Technologies B.V.
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