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Rare disease

Alexander disease

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1 Clinical trial

Alexander disease

Not recruiting
Investigational
Countries:ItalyItaly
  • Participants:0–17 years · 18–64 years
  • Substances:2'-O-(2-Methoxyethyl)-D-Ribose Antisense Oligonucleotide Targeting Glial Fibrillary Acidic Protein Messenger Ribonucleic Acid
  • Sponsor:Ionis Pharmaceuticals Inc.
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