Not recruiting
Alexander disease
Not recruitingInvestigational
Study of ION373 Given by Spinal Injection for Patients with Alexander Disease
Investigational
- Disease:Alexander disease
- Substances:2'-O-(2-Methoxyethyl)-D-Ribose Antisense Oligonucleotide Targeting Glial Fibrillary Acidic Protein Messenger Ribonucleic Acid
Countries:
Italy
Italy- Participants:0–17 years · 18–64 years
- Substances:2'-O-(2-Methoxyethyl)-D-Ribose Antisense Oligonucleotide Targeting Glial Fibrillary Acidic Protein Messenger Ribonucleic Acid
- Sponsor:Ionis Pharmaceuticals Inc.

