Recruiting
Combined immunodeficiency
RecruitingInvestigationalNo placebo
Study on Gene Therapy for Severe Combined Immunodeficiency (SCID) Using ARTEGENE in Patients with Artemis Gene Mutations
InvestigationalNo placebo
- Disease:Combined immunodeficiency
- Substances:Autologous Cd34+ Haematopoietic Stem And Progenitor Cells Transduced With A Lentiviral Vector Containing The Human Dclre1C Gene
Countries:
France
France- Participants:0–17 years
- Substances:Autologous Cd34+ Haematopoietic Stem And Progenitor Cells Transduced With A Lentiviral Vector Containing The Human Dclre1C Gene
- Sponsor:Assistance Publique Hopitaux De Paris
