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Rare disease

Facioscapulohumeral muscular dystrophy

  • 8 clinical trials
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8 Clinical trials

Countries:DenmarkDenmark
  • Participants:18–64 years · 65+ years
  • Substances:Humanised Igg1 Monoclonal Antibody Against Tfr1 Conjugated To Double Stranded Sirna Oligonucleotide Against Dux4 Mrna Via A Non-Cleavable Linker
  • Sponsor:Avidity Biosciences Inc.
Registered drug
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years
  • Substances:Ads-010
  • Sponsor:Sarepta Therapeutics Inc.
Countries:DenmarkDenmark
  • Participants:18–64 years · 65+ years
  • Substances:Losmapimod
  • Sponsor:Fulcrum Therapeutics Inc.
Countries:DenmarkDenmark
  • Participants:18–64 years
  • Substances:Humanised Igg1 Monoclonal Antibody Against Human Latent Myostatin
  • Sponsor:F. Hoffmann-La Roche AG
Countries:FranceFrance
  • Participants:18–64 years · 65+ years
  • Substances:Losmapimod
  • Sponsor:Fulcrum Therapeutics Inc.
Countries:The NetherlandsThe Netherlands
  • Participants:18–64 years · 65+ years
  • Substances:Losmapimod
  • Sponsor:Fulcrum Therapeutics Inc.
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