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Rare disease

Gaucher's disease type I

  • 5 clinical trials
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5 Clinical trials

Countries:SpainSpain
  • Participants:18–64 years · 65+ years
  • Substances:Prednisolone
  • Sponsor:Spur Therapeutics Limited

Gaucher's disease type I

Not yet recruiting
Registered drugNo placebo
Countries:GermanyGermany
  • Participants:18–64 years · 65+ years
  • Substances:Eculizumab
  • Sponsor:Prevail Therapeutics Inc.
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Eliglustat Tartrate
  • Sponsor:Genzyme Corp.
Countries:SpainSpain
  • Participants:18–64 years · 65+ years
  • Substances:Adeno-Associated Viral Vector Serotype S3 Containing Codon-Optimised Expression Cassette Encoding Human Beta-Glucocerebrosidase Variant
  • Sponsor:Spur Therapeutics Limited
Countries:GermanyGermany
  • Participants:18–64 years
  • Substances:Imiglucerase
  • Sponsor:Genzyme Corp.
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