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Rare disease

Mucopolysaccharidosis III

  • 4 clinical trials
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4 Clinical trials

Countries:SpainSpain
  • Participants:0–17 years
  • Substances:Rebisufligene Etisparvovec
  • Sponsor:Ultragenyx Pharmaceutical Inc.
Countries:SpainSpain
  • Participants:0–17 years
  • Substances:Rebisufligene Etisparvovec
  • Sponsor:Ultragenyx Pharmaceutical Inc.
Countries:SpainSpain
  • Participants:0–17 years
  • Substances:Adeno-Associated Viral Vector Serotype 9 Containing The Human Sulfamidase Gene
  • Sponsor:Esteve Pharmaceuticals S.A.
Countries:GermanyGermany
  • Participants:0–17 years
  • Substances:N-Sulfoglucosamine Sulfohydrolase Fused To A Humanised Monoclonal Antibody Targeting Human Transferrin Receptor
  • Sponsor:Jcr Pharmaceuticals Co. Ltd.
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