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Rare disease

Osteochondrodysplasia

  • 12 clinical trials
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12 Clinical trials

Registered drugNo placebo
Countries:ItalyItaly
  • Participants:0–17 years
  • Substances:Vosoritide
  • Sponsor:Biomarin Pharmaceutical Inc.
Countries:NorwayNorway
  • Participants:0–17 years
  • Substances:Infigratinib
  • Sponsor:Qed Therapeutics Inc.
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Infigratinib
  • Sponsor:Qed Therapeutics Inc.
Countries:AustriaAustria
  • Participants:0–17 years
  • Sponsor:Ascendis Pharma Growth Disorders A/S
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