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Rare disease

Severe myoclonic epilepsy of infancy

  • 11 clinical trials
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11 Clinical trials

Countries:FranceFrance
  • Participants:18–64 years · Healthy volunteers
  • Substances:4-Fluoro-N-[2-[4-(2-Methoxyphenyl)Piperazin-1-Yl]Ethyl]-N-Pyridin-2-Ylbenzamide
  • Sponsor:Hospices Civils De Lyon
Investigational
Countries:HungaryHungary
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Clemizole Hydrochloride
  • Sponsor:Epygenix Therapeutics Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years
  • Sponsor:Ionis Pharmaceuticals Inc.
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:ZOREVUNERSEN SODIUM
  • Sponsor:Stoke Therapeutics Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years · 65+ years
  • Sponsor:Longboard Pharmaceuticals Inc.
Countries:ItalyItaly
  • Participants:0–17 years · 18–64 years
  • Substances:Fenfluramine Hydrochloride
  • Sponsor:Zogenix International Limited
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