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Rare disease

Sickle cell anaemia

  • 13 clinical trials
  • 6 recruiting
  • 7 countries
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13 Clinical trials

Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Etavopivat
  • Sponsor:Novo Nordisk A/S
Countries:BelgiumBelgium
  • Participants:18–64 years · 65+ years
  • Substances:Lidocaine Hydrochloride
  • Sponsor:CHU Saint Pierre
Countries:FranceFrance
  • Participants:18–64 years · 65+ years
  • Substances:Iohexol
  • Sponsor:Centre Hospitalier Regional Universitaire De Tours
Countries:GermanyGermany
  • Participants:0–17 years
  • Substances:Busulfan
  • Sponsor:Vertex Pharmaceuticals Inc.
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years
  • Substances:Exagamglogene Autotemcel
  • Sponsor:Vertex Pharmaceuticals Inc.
Countries:GermanyGermany
  • Participants:0–17 years · 18–64 years
  • Substances:Busulfan
  • Sponsor:Vertex Pharmaceuticals Inc.
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