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Rare disease

Thalassaemia alpha

  • 4 clinical trials
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4 Clinical trials

Countries:DenmarkDenmark
  • Participants:18–64 years
  • Substances:(S)-4,5-Dihydro-2-[2-Hydroxy-4-(3,6-Dioxaheptyloxy)Phenyl]-4-Methyl-4-Thiazolecarboxylic Acid
  • Sponsor:Pharmacosmos A/S
Countries:GreeceGreece
  • Participants:0–17 years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.

Thalassaemia beta+2

Not yet recruiting
Investigational
Countries:GreeceGreece
  • Participants:0–17 years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.

Thalassaemia alpha

Not recruiting
Registered drug
Countries:GreeceGreece
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Luspatercept
  • Sponsor:Celgene Corp.
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