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Agios Pharmaceuticals Inc.
Sponsor

Agios Pharmaceuticals Inc.

United States 88 Sidney Street, 02139-4137, United States

About the sponsor

The sponsor demonstrates significant commitment to advancing treatment options for patients with acute myeloid leukemia and myelodysplastic syndromes. Research initiatives focus on addressing relapsed or refractory disease in adult populations, with particular attention to patients who have exhausted standard therapeutic options. The investigational approaches target specific molecular pathways involved in hematologic malignancies, exploring novel mechanisms that may offer clinical benefit to patients with limited treatment alternatives.

  • Acute Myeloid Leukemia
  • Myelodysplastic Syndromes
  • Relapsed or Refractory Hematologic Cancers

The research portfolio includes trials designed to evaluate therapeutic efficacy in patients who have previously received multiple lines of therapy, addressing a critical unmet need in refractory hematologic conditions.

About Specializations

Agios Pharmaceuticals Inc. runs clinical trials in conditions such as Thalassaemia, Anaemia, Thalassaemia beta, Thalassaemia alpha, among others.

All trials

Ongoing trials

Clinical trials registered by this sponsor – none is enrolling right now.

Condition
Country
City
Type of trial
Recruitment status
Quick filters

11 clinical trials

Anaemia

Not yet recruiting
Investigational
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.
Countries:GreeceGreece
  • Participants:0–17 years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.

Thalassaemia beta+2

Not yet recruiting
Investigational
Countries:GreeceGreece
  • Participants:0–17 years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.

Sickle cell disease

Not recruiting
Investigational
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Ag-946 Phosphate
  • Sponsor:Agios Pharmaceuticals Inc.
Countries:BulgariaBulgaria
  • Participants:18–64 years · 65+ years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.

Thalassaemia

Not recruiting
Investigational
Countries:BulgariaBulgaria
  • Participants:18–64 years · 65+ years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.
Countries:CzechiaCzechia
  • Participants:0–17 years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.

Anaemia

Not recruiting
Investigational
Countries:BelgiumBelgium
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.
Countries:FranceFrance
  • Participants:0–17 years · 18–64 years · 65+ years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.
Countries:FranceFrance
  • Participants:0–17 years
  • Substances:Mitapivat
  • Sponsor:Agios Pharmaceuticals Inc.
Countries:AustriaAustria
  • Participants:18–64 years · 65+ years
  • Substances:Ag-946
  • Sponsor:Agios Pharmaceuticals Inc.

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